Percentage of Participants Who Reached ≥10% Weight Loss Threshold After 1 Year (Pivotal Cohort)
| Group | Value (percentage of participants) |
|---|---|
| Setmelanotide (Entire Study) | 80.0 |
Trial · Interventional
CompletedPhase 3Results postedRegistry dataUnited States, Belgium, Canada, France, Germany, Spain, United Kingdom
1 trial · 1 completed · 1 with posted results
Setmelanotide for the Treatment of Early-Onset Pro-Opiomelanocortin (POMC) Deficiency Obesity
NCT0289619214 Feb 2017 to 25 May 2020
Text and fields below are the sponsor's entries at ClinicalTrials.gov, shown as posted.
To demonstrate statistically significant and clinically meaningful effects of setmelanotide on percent body weight change in participants with pro-opiomelanocortin (POMC) deficiency or proprotein convertase subtilisin/kexin type 1 (PCSK1) deficiency obesity due to rare biallelic or loss-of function mutations at the end of 1 year of treatment.
Experimental
Setmelanotide
Participants received titrated doses of setmelanotide once daily, by subcutaneous (SC) injection during titration period for 2 - 12 weeks. Thereafter, participants continued setmelanotide at their specific therapeutic dose for an additional 10 weeks during the open label treatment period. Participants who achieved at least a 5 kilograms (kg) weight loss (or at least 5% weight loss if baseline body weight was \<100 kg) at the end of the open label treatment period, continued into the 8-week double-blind withdrawal period and received 4 weeks setmelanotide and 4 weeks placebo. Following the withdrawal period, participants entered open label treatment period and received setmelanotide to complete approximately 52 weeks (\~1 year) of treatment at a therapeutic dose.
Outcomes the sponsor listed as primary.
Percentage of Participants Who Reached ≥10% Weight Loss Threshold After 1 Year (Pivotal Cohort)
Time frame · Week 52
The percentage of participants who met the ≥ 10% weight loss threshold after approximately Week 52 (\~1 year) of treatment were analyzed.
Percentage of Participants Who Reached ≥10% Weight Loss Threshold After 1 Year (Pivotal + Supplemental Cohort)
Time frame · Week 52
The percentage of participants who met the ≥ 10% weight loss threshold after approximately Week 52 (\~1 year) of treatment were analyzed.
Mean Percent Change From Baseline in Body Weight at Week 52
Time frame · Baseline, Week 52
The mean percent change from baseline in body weight at 52 weeks was analyzed.
Mean Percent Change From Baseline in Hunger Score (Worst "Most" Hunger in 24 Hours) at Week 52
Time frame · Baseline, Week 52
The mean percent change in hunger scores for participants ≥12 years of age with leptin receptor (LEPR) deficiency obesity in treatment with setmelanotide was evaluated. Hunger score ranged from 0 - 10 on a Likert-type scale; 0 = not hungry at all and 10 = hungriest possible. On the Daily Hunger Questionnaire, each of the 3 items (average hunger, most/worst hunger, and morning hunger) was scored separately and averaged on a weekly basis. The weekly average hunger score of the daily worst (most) hunger score in 24 hours is the hunger score used to assess this study endpoint.
Percentage of Participants Who Achieved at Least 25% Improvement in Daily Hunger From Baseline
Time frame · Baseline, Week 52
The percentage of participants (≥12 years of age) achieving a ≥25% improvement from baseline in hunger score at Week 52 (i.e., after treatment with setmelanotide for 52 weeks at the therapeutic dose) was assessed. Hunger ranged from 0 - 10 on a Likert-type scale; 0 = not hungry at all and 10 = hungriest possible. On the Daily Hunger Questionnaire, each of the 3 items (average hunger, most/worst hunger, and morning hunger) was scored separately and averaged on a weekly basis. The weekly average hunger score of the daily worst (most) hunger score in 24 hours is the hunger score used to assess this study endpoint.
Absolute Change From Baseline in Waist Circumference at Week 52
Time frame · Baseline, Week 52
Waist circumference (centimeters) was measured according to the National Heart, Lung, and Blood Institute (NHLBI) criteria. Waist circumference was measured when participants were fasting at approximately the same time at each visit. The absolute change from baseline in waist circumference was assessed.
Absolute Change in Body Weight (Reversal of Weight Loss) During Double-Blind Placebo-Controlled Withdrawal Period
Time frame · Baseline, 8-week withdrawal period (up to ~Week 20)
A comparison of weight change was evaluated during the 8 week placebo-controlled withdrawal period for each participant, during which each participant received 4 weeks of placebo and 4 weeks active therapy in a blinded fashion.
Absolute Score in Daily Hunger Reduction During the Double-Blind Placebo-Controlled Withdrawal Period
Time frame · 8-week withdrawal period (up to ~Week 20)
The absolute score in daily hunger during the double-blind placebo-controlled withdrawal period (≥12 Years of Age) was assessed. Hunger ranged from 0 - 10 on a Likert-type scale; 0 = not hungry at all and 10 = hungriest possible. On the Daily Hunger Questionnaire, each of the 3 items (average hunger, most/worst hunger, and morning hunger) was scored separately and averaged on a weekly basis. The weekly average hunger score of the daily worst (most) hunger score in 24 hours is the hunger score used to assess this study endpoint. Lower scores represent lower hunger, higher scores represent greater hunger.
Mean Percent Change From Baseline in Body Mass Index (BMI) at Week 52
Time frame · Baseline, Week 52
The mean percent change from baseline in BMI was assessed.
Area Under the Curve (AUC) Change From Baseline in Oral Glucose, Assessed by the Oral Glucose Tolerance Test (OGTT)
Time frame · Baseline, Week 52
The AUC change from baseline for the OGTT was assessed. The AUC was calculated by the linear trapezoidal method and includes pre-dose and post-dose assessments. At each visit, oral glucose was captured pre-meal, and post-meal at the following times: 30 minutes, 60 minutes, 90 minutes, and 120 minutes. OGTT was not performed for participants with a diagnosis of Type 1 or Type 2 diabetes.
Change From Baseline in Serum Glucose at Week 52
Time frame · Baseline, Week 52
Change from baseline in serum glucose at Week 52 was assessed.
Values are shown as posted at ClinicalTrials.gov, with their units. PepBank has not converted, pooled or compared them.
| Group | Value (percentage of participants) |
|---|---|
| Setmelanotide (Entire Study) | 80.0 |
| Group | Value (percentage of participants) |
|---|---|
| Setmelanotide (Entire Study) | 85.7 |
| Group | Value (percent change) | Spread |
|---|---|---|
| Setmelanotide (Entire Study) | -25.83 | 9.721 |
| Group | Value (percent change) | Spread |
|---|---|---|
| Setmelanotide (Entire Study) | -27.1 | 28.11 |
| Group | Value (percentage of participants) |
|---|---|
| Setmelanotide (Entire Study) | 50.0 |
| Group | Value (centimeters) | Spread |
|---|---|---|
| Setmelanotide (Entire Study) | 115.48 | 17.920 |
| Group | Value (kilograms) | Spread |
|---|---|---|
| Setmelanotide (Double-Blind) | -2.8 | 2.41 |
| Group | Value (units on a scale) | Spread |
|---|---|---|
| Setmelanotide (Double-Blind) | 4.5 | 2.57 |
| Group | Deaths | Serious events | Other events |
|---|---|---|---|
| SetmelanotideParticipants received titrated doses of setmelanotide once daily, by SC injection during titration period for 2 - 12 weeks. Thereafter, participants continued setmelanotide at their specific therapeutic dose for an additional 10 weeks during the open label treatment period. Participants who achieved at least a 5 kg weight loss (or at least 5% weight loss if baseline body weight was \<100 kg) at the end of the open label treatment period, continued into the 8-week double-blind withdrawal period and received 4 weeks setmelanotide and 4 weeks placebo. Following the withdrawal period, participants entered open label treatment period and received setmelanotide to complete approximately 52 weeks (\~1 year) of treatment at a therapeutic dose. | 0 / 15 | 6 / 15 | 15 / 15 |
Each cell reads participants affected / participants at risk, as the registry posted them.
Registry data comes from ClinicalTrials.gov. Study results come from studies, not from the registry. How PepBank works
Studies that cite this trial.
1 study on this page
PubMed tag: none · 2026
Clément et al. 2026Advances in therapy
PMID 42821228DOI 10.1007/s12325-026-03741-xPUB-42821228
Indexing hint: Clinical trial · 2020
Clément et al. 2020The lancet. Diabetes & endocrinologycited by 363
PMID 33137293DOI 10.1016/s2213-8587(20)30364-8PUB-33137293
Who could join, as posted.
PepBank is a research reference. Talk to a doctor before you use any peptide.
In PepBank now:147 peptides, 6 blends and 13 other compounds97,577 study results from 17,383 studies8,473 clinical trialsUpdated